REGENXBIO, founded in 2008, is a clinical-stage biotechnology company based in the United States known for its pioneering work in AAV Therapeutics, a promising class of gene therapy medicines. The company is actively advancing a robust pipeline targeting retinal and rare diseases with products like ABBV-RGX-314 in collaboration with AbbVie, RGX-202 for Duchenne, and RGX-121 for MPS II. These treatments, potentially one-time therapies, could revolutionize healthcare for millions globally.
With its innovative platform, REGENXBIO has impacted thousands of patients, including those treated with Novartis’ ZOLGENSMA for spinal muscular atrophy. The company is continually attracting substantial investments, most recently securing a $250.00M post-IPO debt financing from HealthCare Royalty Partners as of 01 May 2025. This investment positions REGENXBIO for promising future growth in the biopharma and biotechnology sectors.